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36 results
Medicine
Orphan designations Remove Orphan designations filter
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Orphan designation status
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Orphan designation: Refusal of orphan designation for the treatment of acute uncomplicated plasmodium falciparum malaria
Date of refusal of designation: 26/07/2002, Negative, Last updated: 08/01/2003 -
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Orphan designation: Refusal of orphan designation for the treatment of non-traumatic subarachnoid haemorrhage
Date of refusal of designation: 15/03/2018, Negative, Last updated: 11/10/2018 -
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Orphan designation: Refusal of orphan designation for the treatment of oculopharyngeal muscular dystrophy
Date of refusal of designation: 13/04/2018, Negative, Last updated: 11/01/2019 -
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Orphan designation: Refusal of orphan designation for the treatment of epidermolysis bullosa
Date of refusal of designation: 08/11/2018, Negative, Last updated: 14/06/2019 -
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Orphan designation: Refusal of orphan designation for the treatment of fibromyalgia
Date of refusal of designation: 07/11/2020, Negative, Last updated: 24/02/2020 -
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Orphan designation: Refusal of orphan designation for the treatment of hepatocellular carcinoma
Date of refusal of designation: 23/09/2019, Negative, Last updated: 06/05/2020 -
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Orphan designation: Refusal of orphan designation for the treatment of intracerebral haemorrhage
Date of refusal of designation: 06/07/2020, Negative, Last updated: 19/11/2020 -
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Orphan designation: Refusal of orphan designation for the treatment of eumycetoma
Date of refusal of designation: 18/06/2020, Negative, Last updated: 19/11/2020 -
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Orphan designation: Refusal of orphan designation for the treatment of non-small cell lung cancer with EGFR alterations
Date of refusal of designation: 28/06/2021, Negative, Last updated: 24/01/2022 -
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Orphan designation: Refusal of orphan designation for the prevention of spaceflight-related radiation and microgravity
Date of refusal of designation: 14/10/2022, Negative, Last updated: 23/01/2023 -
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Orphan designation: Refusal of orphan designation for the treatment of retinopathy of prematurity
Date of refusal of designation: 28/11/2022, Negative, Last updated: 23/01/2023