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4 results
Medicine
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Orphan designation: for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 16/06/2005, Expired, Last updated: 03/10/2017 -
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Orphan designation: for: Treatment of primary insulin-like growth factor-1 deficiency due to molecular or genetic defects
Date of first decision: 22/05/2006, Expired, Last updated: 03/10/2017 -
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Orphan designation: for: Treatment of mucopolysaccharidosis type II (Hunter's syndrome)
Date of first decision: 11/12/2001, Expired, Last updated: 08/02/2017 -
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Orphan designation: for: Treatment of mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)
Date of first decision: 15/02/2001, Expired, Last updated: 10/02/2016