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56 results
Medicine
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Orphan designation: dasatinib for: Treatment of chronic myeloid leukaemia
Date of first decision: 23/12/2005, Expired, Last updated: 08/02/2017 -
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Orphan designation: 4-(3,5-Bis(hydroxy-phenyl)-1,2,4) triazol-1-yl) benzoic acid for: Treatment of chronic iron overload requiring chelation therapy
Date of first decision: 13/03/2002, Expired, Last updated: 30/09/2016 -
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Orphan designation: Dexrazoxane for: Treatment of anthracycline extravasations
Date of first decision: 19/09/2001, Expired, Last updated: 30/09/2016 -
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Orphan designation: 2-Chloro-9-[2-deoxy-2-fluoro-ß-D-arabinofuranosyl]adenine for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 05/02/2002, Expired, Last updated: 10/08/2016 -
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Orphan designation: Sorafenib tosylate for: Treatment of renal-cell carcinoma
Date of first decision: 29/07/2004, Expired, Last updated: 10/08/2016 -
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Orphan designation: Recombinant human acid alpha-glucosidase for: Treatment of glycogen storage disease type II (Pompe's disease)
Date of first decision: 15/02/2001, Expired, Last updated: 10/08/2016 -
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Orphan designation: N-acetylgalactosamine 4-sulfatase for: Treatment of mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)
Date of first decision: 15/02/2001, Expired, Last updated: 10/02/2016 -
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Orphan designation: sildenafil citrate for: Treatment of pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension
Date of first decision: 12/12/2003, Expired, Last updated: 19/01/2016 -
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Orphan designation: nitisinone for: Treatment of tyrosinaemia type 1
Date of first decision: 30/12/2000, Expired, Last updated: 08/05/2015 -
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Orphan designation: ziconotide for: Treatment of chronic pain requiring intraspinal analgesia
Date of first decision: 09/07/2001, Expired, Last updated: 08/05/2015 -
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Orphan designation: Zinc acetate dihydrate for: Treatment of Wilson's disease
Date of first decision: 31/07/2001, Expired, Last updated: 06/03/2015 -
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Orphan designation: Ibuprofen for: Treatment of patent ductus arteriosus
Date of first decision: 15/02/2001, Expired, Last updated: 06/03/2015 -
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Orphan designation: imatinib mesilate for: Treatment of chronic myeloid leukaemia
Date of first decision: 15/02/2001, Expired, Last updated: 10/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 26/08/2005, Expired, Last updated: 10/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of malignant gastrointestinal stromal tumours
Date of first decision: 20/11/2001, Expired, Last updated: 09/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of myelodysplastic / myeloproliferative diseases
Date of first decision: 23/12/2005, Expired, Last updated: 09/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of dermatofibrosarcoma protuberans
Date of first decision: 26/08/2005, Expired, Last updated: 09/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of chronic eosinophilic leukaemia and the hypereosinophilic syndrome
Date of first decision: 28/10/2005, Expired, Last updated: 09/02/2015 -
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Orphan designation: N-carbamyl-L-glutamic acid for: Treatment of N-acetylglutamate synthetase (NAGS) deficiency
Date of first decision: 18/10/2000, Expired, Last updated: 25/07/2014 -
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Orphan designation: Mitotane for: Treatment of adrenal cortical carcinoma
Date of first decision: 12/06/2002, Expired, Last updated: 19/06/2014 -
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Orphan designation: Cladribine for: Treatment of indolent non-Hodgkin's lymphoma
Date of first decision: 18/09/2001, Expired, Last updated: 18/06/2014 -
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Orphan designation: Arsenic trioxide for: Treatment of acute promyelocytic leukaemia
Date of first decision: 18/10/2000, Expired, Last updated: 17/10/2013 -
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Orphan designation: iloprost for: Treatment of primary and of the following forms of secondary pulmonary hypertension…
Date of first decision: 30/12/2000, Expired, Last updated: 08/10/2013 -
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Orphan designation: busulfan for: Conditioning treatment prior to haematopoietic-progenitor-cell transplantation
Date of first decision: 30/12/2000, Expired, Last updated: 31/07/2013 -
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Orphan designation: laronidase for: Treatment of mucopolysaccharidosis type I
Date of first decision: 15/02/2001, Expired, Last updated: 08/07/2013