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257 results
Medicine
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Summary of opinion: Zynlonta (updated)
loncastuximab tesirine, opinion date: 15/09/2022, Positive, Last updated: 19/09/2022 -
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Summary of opinion: Retsevmo
selpercatinib, opinion date: 22/04/2022, Positive, Last updated: 22/04/2022 -
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Summary of opinion: Crysvita
burosumab, opinion date: 23/06/2022, Positive, Last updated: 24/06/2022 -
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Summary of opinion: Ultomiris
ravulizumab, opinion date: 21/07/2022, Positive, Last updated: 22/07/2022 -
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Summary of opinion: Tecartus
Autologous peripheral blood T cells CD4 and CD8 selected and CD3 and CD28 activated transduced with retroviral vector expressing anti-CD19 CD28/CD3-zeta chimeric antigen receptor and cultured, opinion date: 21/07/2022, Positive, Last updated: 22/07/2022 -
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Summary of opinion: Retsevmo
selpercatinib, opinion date: 21/07/2022, Positive, Last updated: 22/07/2022 -
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Summary of opinion: Adtralza (new)
tralokinumab, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Skyrizi (new)
risankizumab, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Biktarvy (new)
bictegravir, emtricitabine, tenofovir alafenamide, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Brukinsa (new)
zanubrutinib, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Vaxneuvance (new)
pneumococcal polysaccharide conjugate vaccine (adsorbed), opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Pyrukynd (new)
mitapivat, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Yescarta (new)
axicabtagene ciloleucel, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Enjaymo (new)
sutimlimab, opinion date: 15/09/2022, Positive, Last updated: 16/09/2022 -
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Summary of opinion: Vegzelma
bevacizumab, opinion date: 23/06/2022, Positive, Last updated: 21/06/2022 -
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Summary of opinion: Imcivree
setmelanotide, opinion date: 21/07/2022, Positive, Last updated: 22/07/2022 -
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Orphan designation: Recombinant human IgG1 kappa light chain monoclonal antibody targeting plasma kallikrein (lanadelumab) for: Treatment of hereditary angioedema (updated)
Date of designation: 09/10/2015, Positive, Last updated: 04/10/2022 -
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Orphan designation: Recombinant human parathyroid hormone for: Treatment of hypoparathyroidism (updated)
Date of designation: 16/01/2014, Positive, Last updated: 04/10/2022 -
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Orphan designation: Maribavir for: Prevention of cytomegalovirus disease in patients with impaired cell-mediated immunity (updated)
Date of designation: 18/12/2007, Positive, Last updated: 04/10/2022 -
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Orphan designation: Setmelanotide for: Treatment of Bardet-Biedl syndrome (updated)
Date of designation: 21/08/2019, Positive, Last updated: 30/09/2022 -
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Orphan designation: Cyclic pyranopterin monophosphate (fosdenopterin) for: Treatment of molybdenum-cofactor deficiency type A (updated)
Date of designation: 20/09/2010, Positive, Last updated: 30/09/2022 -
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Orphan designation: Adeno-associated viral vector serotype 5 containing a B-domain deleted variant of human coagulation factor VIII gene for: Treatment of haemophilia A (updated)
Date of designation: 21/03/2016, Positive, Last updated: 28/09/2022 -
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Orphan designation: budesonide for: Treatment of primary IgA nephropathy (updated)
Date of designation: 18/11/2016, Positive, Last updated: 14/09/2022 -
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Orphan designation: Efgartigimod alfa for: Treatment of myasthenia gravis (updated)
Date of designation: 10/08/2022, Positive, Last updated: 12/09/2022 -
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Orphan designation: Asciminib for: Treatment of chronic myeloid leukaemia (updated)
Date of designation: 24/03/2020, Positive, Last updated: 07/09/2022