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Orphan designation: S-[5-(omega-methoxypoly(oxyethylene)-2-oxopentyl)]-L-cysteinylglycyl-L-serinylglycylgylcyl-L-isoleucyl-L-lysyl-L-glutamyl-L-phenylalanyl-L-leucyl-L-glutaminyl-L-arginyl-L-phenylalanyl-L-isoleucyl-L-histyl-L-isoleucyl-L-valyl-L-glutaminyl-L-serinyl-L-isoleucyl-L-isoleucyl-L-asparaginyl-L-threonyl-L-serinamide, acetate salt for: Treatment of cutaneous T-cell lymphoma
Date of designation: 13/04/2021, Positive, Last updated: 21/01/2022 -
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Orphan designation: Cevostamab for: Treatment of multiple myeloma
Date of designation: 13/04/2021, Positive, Last updated: 24/01/2022 -
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Orphan designation: ganglioside GM1 for: Treatment of amyotrophic lateral sclerosis
Date of designation: 13/04/2021, Positive, Last updated: 24/01/2022