For help on how to get the results you want, see our search tips.
2831 results
Categories
Human Remove Human filter
-
List item
Orphan designation: perflubron for: Treatment of respiratory distress syndrome
Date of designation: 09/12/2020, Positive, Last updated: 16/09/2021 -
List item
Orphan designation: Sulindac for: Treatment of fragile X syndrome
Date of designation: 09/12/2020, Positive, Last updated: 12/10/2021 -
List item
Orphan designation: Bovactant for: Treatment of respiratory distress syndrome
Date of designation: 24/02/2022, Positive, Last updated: 29/04/2022 -
List item
Orphan designation: Gadolinium-chelated polysiloxane nanoparticles for: Treatment of pancreatic cancer
Date of designation: 24/02/2022, Positive, Last updated: 29/04/2022 -
List item
Orphan designation: [Ala1,3,12,Gln10,Arg11,Trp14]PTH(1-14)/[Ala18,22, Lys26]PTHrP(15-36)COOH for: Treatment of hypoparathyroidism
Date of designation: 24/02/2022, Positive, Last updated: 29/04/2022 -
List item
Orphan designation: aldesleukin for: Treatment of amyotrophic lateral sclerosis
Date of designation: 24/02/2022, Positive, Last updated: 29/04/2022 -
List item
Orphan designation: Eltanexor for: Treatment of myelodysplastic syndromes
Date of designation: 21/06/2022, Positive, Last updated: 22/09/2022 -
List item
Orphan designation: Octreotide acetate for: Treatment of carcinoid syndrome
Date of designation: 13/01/2023, Positive, Last updated: 23/03/2023 -
List item
Orphan designation: Govorestat for: Treatment of galactosaemia
Date of designation: 21/06/2022, Positive, Last updated: 10/05/2023 -
List item
Orphan designation: epcoritamab for: Treatment of follicular lymphoma
Date of designation: 21/06/2022, Positive, Last updated: 22/09/2022 -
List item
Orphan designation: Sodium phenylbutyrate for: Treatment of ornithine-transcarbamylase deficiency
Date of designation: 09/02/2012, Withdrawn, Last updated: 09/10/2013 -
List item
Orphan designation: Heterologous human adult liver-derived progenitor cells for: Treatment of argininosuccinic aciduria
Date of designation: 17/07/2013, Positive,