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16 results
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Orphan designation: for: Treatment of multiple myeloma
Date of first decision: 20/11/2001, Withdrawn, Last updated: 18/07/2018 -
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Orphan designation: for: Treatment of GNE myopathy
Date of first decision: 16/10/2015, Withdrawn, Last updated: 13/06/2018 -
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Orphan designation: for: Diagnosis of positive folate-receptor status in ovarian cancer
Date of first decision: 10/09/2012, Withdrawn, Last updated: 07/02/2017 -
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Orphan designation: for: Treatment of ovarian cancer
Date of first decision: 09/02/2012, Withdrawn, Last updated: 21/10/2016 -
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Orphan designation: for: Treatment of pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension
Date of first decision: 21/10/2004, Withdrawn, Last updated: 30/09/2016 -
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Orphan designation: for: Treatment of chronic myeloid leukaemia
Date of first decision: 02/09/2004, Withdrawn, Last updated: 10/08/2016 -
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Orphan designation: for: Treatment of invasive fungal infections
Date of first decision: 05/12/2001, Withdrawn, Last updated: 12/02/2015 -
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Orphan designation: for: Treatment of angioedema
Date of first decision: 18/12/2002, Withdrawn, Last updated: 16/10/2014 -
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Orphan designation: for: Treatment of chronic non-infectious uveitis
Date of first decision: 14/09/2007, Withdrawn, Last updated: 17/10/2013 -
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Orphan designation: for: Treatment of acute promyelocytic leukaemia
Date of first decision: 24/07/2009, Withdrawn, Last updated: 31/07/2013 -
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Orphan designation: for: Treatment of high-grade dysplasia in Barrett's oesophagus
Date of first decision: 06/03/2002, Withdrawn, Last updated: 20/06/2013 -
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Orphan designation: for: Treatment of cutaneous T-cell lymphoma
Date of first decision: 21/06/2004, Withdrawn, -
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Orphan designation: for: Treatment of idiopathic thrombocytopenic purpura
Date of first decision: 03/08/2007, Withdrawn, Last updated: 12/01/2012 -
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Orphan designation: for: Treatment of lupus nephritis
Date of first decision: 20/11/2001, Withdrawn, Last updated: 31/05/2011 -
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Orphan designation: for: Treatment of angioedema caused by C1 inhibitor deficiency
Date of first decision: 11/05/2001, Withdrawn, -
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Orphan designation: for: Treatment of growth hormone (GH) gene deletion who have developed neutralizing antibodies to GH
Date of first decision: 20/06/2006, Withdrawn, Last updated: 02/04/2009