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26 results
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Orphan designation: for: Treatment of hepatocellular carcinoma
Date of first decision: 11/04/2006, Expired, Last updated: 31/01/2018 -
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Orphan designation: for: Intra-operative photodynamic diagnosis of residual glioma
Date of first decision: 14/11/2002, Expired, Last updated: 03/10/2017 -
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Orphan designation: for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 16/06/2005, Expired, Last updated: 03/10/2017 -
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Orphan designation: for: Treatment of primary insulin-like growth factor-1 deficiency due to molecular or genetic defects
Date of first decision: 22/05/2006, Expired, Last updated: 03/10/2017 -
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Orphan designation: for: Treatment of sickle cell syndrome
Date of first decision: 09/07/2003, Expired, Last updated: 06/08/2017 -
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Orphan designation: for: Treatment of severe myoclonic epilepsy in infancy
Date of first decision: 06/12/2001, Expired, Last updated: 08/02/2017 -
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Orphan designation: for: Treatment of mucopolysaccharidosis type II (Hunter's syndrome)
Date of first decision: 11/12/2001, Expired, Last updated: 08/02/2017 -
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Orphan designation: for: Treatment of essential thrombocythaemia
Date of first decision: 30/12/2000, Expired, Last updated: 08/02/2017 -
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Orphan designation: for: Treatment of chronic iron overload requiring chelation therapy
Date of first decision: 13/03/2002, Expired, Last updated: 30/09/2016 -
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Orphan designation: for: Treatment of renal-cell carcinoma
Date of first decision: 29/07/2004, Expired, Last updated: 10/08/2016 -
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Orphan designation: for: Treatment of glycogen storage disease type II (Pompe's disease)
Date of first decision: 15/02/2001, Expired, Last updated: 10/08/2016 -
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Orphan designation: for: Treatment of mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)
Date of first decision: 15/02/2001, Expired, Last updated: 10/02/2016 -
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Orphan designation: for: Treatment of pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension
Date of first decision: 12/12/2003, Expired, Last updated: 19/01/2016 -
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Orphan designation: for: Treatment of chronic pain requiring intraspinal analgesia
Date of first decision: 09/07/2001, Expired, Last updated: 08/05/2015 -
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Orphan designation: for: Treatment of tyrosinaemia type 1
Date of first decision: 30/12/2000, Expired, Last updated: 08/05/2015 -
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Orphan designation: for: Treatment of patent ductus arteriosus
Date of first decision: 15/02/2001, Expired, Last updated: 06/03/2015 -
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Orphan designation: for: Treatment of Wilson's disease
Date of first decision: 31/07/2001, Expired, Last updated: 06/03/2015 -
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Orphan designation: for: Treatment of N-acetylglutamate synthetase (NAGS) deficiency
Date of first decision: 18/10/2000, Expired, Last updated: 25/07/2014 -
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Orphan designation: for: Treatment of adrenal cortical carcinoma
Date of first decision: 12/06/2002, Expired, Last updated: 19/06/2014 -
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Orphan designation: for: Treatment of indolent non-Hodgkin's lymphoma
Date of first decision: 18/09/2001, Expired, -
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Orphan designation: for: Treatment of acute promyelocytic leukaemia
Date of first decision: 18/10/2000, Expired, Last updated: 17/10/2013 -
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Orphan designation: for: Treatment of primary and of the following forms of secondary pulmonary hypertension…
Date of first decision: 30/12/2000, Expired, Last updated: 08/10/2013 -
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Orphan designation: for: Treatment of mucopolysaccharidosis type I
Date of first decision: 15/02/2001, Expired, Last updated: 08/07/2013 -
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Orphan designation: for: Treatment of acromegaly
Date of first decision: 15/02/2001, Expired, Last updated: 27/02/2013 -
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Orphan designation: for: Treatment of Fabry disease
Date of first decision: 08/08/2000, Expired, Last updated: 18/11/2011