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Orphan designation: imatinib mesilate for: Treatment of chronic myeloid leukaemia
Date of designation: 15/02/2001, Expired, Last updated: 10/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of acute lymphoblastic leukaemia
Date of designation: 26/08/2005, Expired, Last updated: 10/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of malignant gastrointestinal stromal tumours
Date of designation: 20/11/2001, Expired, Last updated: 09/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of myelodysplastic / myeloproliferative diseases
Date of designation: 23/12/2005, Expired, Last updated: 09/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of chronic eosinophilic leukaemia and the hypereosinophilic syndrome
Date of designation: 28/10/2005, Expired, Last updated: 09/02/2015 -
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Orphan designation: imatinib mesilate for: Treatment of dermatofibrosarcoma protuberans
Date of designation: 26/08/2005, Expired, Last updated: 09/02/2015 -
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Orphan designation: N-carbamyl-L-glutamic acid for: Treatment of N-acetylglutamate synthetase (NAGS) deficiency
Date of designation: 18/10/2000, Expired, Last updated: 25/07/2014 -
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Orphan designation: Mitotane for: Treatment of adrenal cortical carcinoma
Date of designation: 12/06/2002, Expired, Last updated: 19/06/2014 -
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Orphan designation: Cladribine for: Treatment of indolent non-Hodgkin's lymphoma
Date of designation: 18/09/2001, Expired, Last updated: 18/06/2014 -
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Orphan designation: Arsenic trioxide for: Treatment of acute promyelocytic leukaemia
Date of designation: 18/10/2000, Expired, Last updated: 17/10/2013 -
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Orphan designation: iloprost for: Treatment of primary and of the following forms of secondary pulmonary hypertension…
Date of designation: 30/12/2000, Expired, Last updated: 08/10/2013 -
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Orphan designation: busulfan for: Conditioning treatment prior to haematopoietic-progenitor-cell transplantation
Date of designation: 30/12/2000, Expired, Last updated: 31/07/2013 -
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Orphan designation: laronidase for: Treatment of mucopolysaccharidosis type I
Date of designation: 15/02/2001, Expired, Last updated: 08/07/2013 -
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Orphan designation: 1,5-(Butylimino)-1,5-dideoxy, D-glucitol for: Treatment of Gaucher disease
Date of designation: 18/10/2000, Expired, Last updated: 27/02/2013 -
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Orphan designation: Bosentan for: Treatment of pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension
Date of designation: 15/02/2001, Expired, Last updated: 27/02/2013 -
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Orphan designation: Pegvisomant for: Treatment of acromegaly
Date of designation: 15/02/2001, Expired, Last updated: 27/02/2013 -
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Orphan designation: Alpha-galactosidase A for: Treatment of Fabry disease
Date of designation: 08/08/2000, Expired, Last updated: 18/11/2011 -
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Orphan designation: Temsirolimus for: Treatment of mantle cell lymphoma
Date of designation: 07/11/2006, Expired, Last updated: 18/11/2011 -
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Orphan designation: Alpha-galactosidase A for: Treatment of Fabry disease
Date of designation: 08/08/2000, Expired, Last updated: 18/11/2011