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On 14 September 2007, orphan designation (EU/3/07/474) was granted by the European Commission to CSL Behring GmbH, Germany, for alpha-1 proteinase inhibitor (inhalation use) for the treatment of cystic fibrosis.

Please note that this product was withdrawn from the Union Register of orphan medicinal products in November 2020 on request of the Sponsor.

Key facts

Active substance
Alpha-1 proteinase inhibitor
Disease / condition
Treatment of cystic fibrosis
Date of first decision
EU designation number

Sponsor's contact details

CSL Behring GmbH
Emil-von-Behring-Str. 76
35041 Marburg
Tel. +49 6421 3912

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

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