On 10 October 2012, orphan designation (EU/3/12/1045) was granted by the European Commission to Grifols Deutschland GmbH, Germany, for alpha-1 proteinase inhibitor (for inhalation use) for the treatment of cystic fibrosis.
Alpha-1 proteinase inhibitor
Treatment of cystic fibrosis
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Review of designation
The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.
Documents related to this orphan designation evaluation
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
EU register of orphan medicines
The list of medicines that have received an orphan designation in the EU is available on the European Commission's website: