EU/3/12/1070

About

On 8 November 2012, orphan designation (EU/3/12/1070) was granted by the European Commission to Advanced Medical Projects, Spain, for recombinant human dyskerin for the treatment of dyskeratosis congenita.

Key facts

Active substance
Recombinant human dyskerin
Disease / condition
Treatment of dyskeratosis congenita
Date of decision
08/11/2012
Outcome
Positive
Orphan decision number
EU/3/12/1070

Review of designation

Sponsor's contact details

Advanced Medical Projects
IIB-CSIC
C/ Arturo Duperier 4
28029 Madrid
Spain
www.advancedmedicalprojects.com/contact/

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

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