On 2 April 2012, orphan designation (EU/3/12/980) was granted by the European Commission to Axcentua Pharmaceuticals AB, Sweden, for genistein sodium salt dihydrate for the treatment of mucopolysaccharidosis type III (Sanfilippo syndrome).
Genistein sodium salt dihydrate
|Disease / condition||
Treatment of mucopolysaccharidosis type III (Sanfilippo syndrome)
|Date of first decision||
|EU designation number||
Review of designation
The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
- Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
- European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.