EU/3/14/1384

About

On 16 December 2014, orphan designation (EU/3/14/1384) was granted by the European Commission to Centre National de la Recherche Scientifique (CNRS), France, for ((E)-1-(4'-chlorophenyl)-3-(4-hydroxy-3-metoxyphenyl)prop-2-en-1-one) for the treatment of WHIM syndrome.

Key facts

Active substance
((E)-1-(4'-chlorophenyl)-3-(4-hydroxy-3-metoxyphenyl)prop-2-en-1-one)
Disease / condition
Treatment of WHIM syndrome
Date of first decision
16/12/2014
Outcome
Positive
EU designation number
EU/3/14/1384

Review of designation

The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.

Sponsor's contact details

Centre National de la Recherche Scientifique (CNRS)
3, rue Michel-Ange
Paris Cedex 16
75794
France
Tel. +33 1 44 96 43 42
E-mail: galzi@unistra.fr

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

How useful was this page?

Add your rating