EU/3/15/1496

About

On 21 May 2015, orphan designation (EU/3/15/1496) was granted by the European Commission to Dr Ulrich Granzer, Germany, for trehalose for the treatment of oculopharyngeal muscular dystrophy.

Key facts

Active substance
Trehalose
Disease / condition
Treatment of oculopharyngeal muscular dystrophy
Date of first decision
21/05/2015
Outcome
Positive
EU designation number
EU/3/15/1496

Review of designation

The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.

Sponsor's contact details

Dr Ulrich Granzer
Mauerkircherstrasse 105
81925 Munich
Germany
Tel. +49 8978 0689820
Fax +49 8978 0689815
E-mail: granzer@granzer.biz

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

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