On 11 November 2015, orphan designation (EU/3/15/1577) was granted by the European Commission to Athena Vision Ltd, United Kingdom, for adenovirus associated viral vector serotype 5 containing the human RPE65 gene for the treatment of Leber's congenital amaurosis.
In September 2016, Athena Vision Ltd changed name to MeiraGTx UK II Limited.
The sponsorship was transferred to MeiraGTx B.V., The Netherlands in May 2019.
Adenovirus associated viral vector serotype 5 containing the human RPE65 gene
|Disease / condition||
Treatment of Leber's congenital amaurosis
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
- European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
- Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;