EU/3/16/1705

About

On 14 July 2016, orphan designation (EU/3/16/1705) was granted by the European Commission to Lucane Pharma SA, France, for sodium benzoate for the treatment of ornithine transcarbamylase deficiency.

Key facts

Active substance
Sodium benzoate
Disease / condition
Treatment of ornithine transcarbamylase deficiency
Date of first decision
14/07/2016
Outcome
Positive
EU designation number
EU/3/16/1705

Review of designation

The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.

Sponsor's contact details

Lucane Pharma SA
172 rue de Charonne
75011 Paris
France
Tel. +33 1 53 86 87 53
Fax +33 1 47 34 56 72
E-mail: info@lucanepharma.com

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

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