EU/3/16/1753

Table of contents

About

On 14 October 2016, orphan designation (EU/3/16/1753) was granted by the European Commission to Centro de Investigación Biomédica en Red, Spain, for haematopoietic stem cells modified with a lentiviral vector containing the CD18 gene for the treatment of leukocyte adhesion deficiency type I.

In October 2017 Centro de Investigación Biomédica en Red (CIBER) changed name to Consorcio Centro de Investigación Biomédica en Red, M.P.

Key facts

Active substance
Haematopoietic stem cells modified with a lentiviral vector containing the CD18 gene
Disease / condition
Treatment of leukocyte adhesion deficiency type I
Date of decision
20/09/2016
Outcome
Positive
Orphan decision number
EU/3/16/1753

Sponsor's contact details

Consorcio Centro de Investigación Biomédica en Red, M.P.
Instituto de Salud Carlos III
Pabellón 11, Planta 0
C/ Monforte de Lemos 3-5
28029 Madrid
Spain
Tel. +34 911 718 114
E-mail: gestores@ciberer.es

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

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