EU/3/17/1845: Orphan designation for the treatment of hereditary haemorrhagic telangiectasia



On 27 February 2017, orphan designation (EU/3/17/1845) was granted by the European Commission to PlumeStars s.r.l., Italy, for thalidomide for the treatment of hereditary haemorrhagic telangiectasia.

Key facts

Active substance
Intended use
Treatment of hereditary haemorrhagic telangiectasia
Orphan designation status
EU designation number
Date of designation
PlumeStars s.r.l.
Strada Inzani 1
43125 Parma
Tel. +39 0521 90 50 86

Review of designation

The Committee for Orphan Medicinal Products reviews the orphan designation of a product it it is approved for marketing authorisation.

Documents related to this orphan designation evaluation

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

EU register of orphan medicines

The list of medicines that have received an orphan designation in the EU is available on the European Commission's website:

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