Overview
On 22 February 2018, orphan designation (EU/3/18/1982) was granted by the European Commission to ATXA Therapeutics Limited, Ireland, for N-(tert-butylcarbamoyl)-5-cyano-2-((4'-(difluoromethoxy)-[1,1'-biphenyl]-3-yl)oxy)benzenesulfonamide (also known as NTP42) for the treatment of pulmonary arterial hypertension.
The sponsor’s address was updated in April 2020.
Key facts
Active substance |
N-(tert-butylcarbamoyl)-5-cyano-2-((4'-(difluoromethoxy)-[1,1'-biphenyl]-3-yl)oxy)benzenesulfonamide
|
Intended use |
Treatment of pulmonary arterial hypertension
|
Orphan designation status |
Positive
|
EU designation number |
EU/3/18/1982
|
Date of designation |
22/02/2018
|
Sponsor |
ATXA Therapeutics Limited |
Patients' organisations
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.
EU register of orphan medicines
The list of medicines that have received an orphan designation in the EU is available on the European Commission's website: