On 31 July 2018, orphan designation (EU/3/18/2042) was granted by the European Commission to MeiraGTx UK II Limited, United Kingdom, for adenovirus associated viral vector serotype 2/8 containing the human CNGA3 gene for the treatment of achromatopsia.
The sponsorship was transferred to MeiraGTx B.V., The Netherlands in May 2019.
The sponsor’s address was updated in July 2021.
Adenovirus associated viral vector serotype 2/8 containing the human CNGA3 gene
Treatment of achromatopsia
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Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.