On 31 July 2018, orphan designation (EU/3/18/2042) was granted by the European Commission to MeiraGTx UK II Limited, United Kingdom, for adenovirus associated viral vector serotype 2/8 containing the human CNGA3 gene for the treatment of achromatopsia.
Adenovirus associated viral vector serotype 2/8 containing the human CNGA3 gene
|Disease / condition||
Treatment of achromatopsia
|Date of decision||
|Orphan decision number||
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
- Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;