EU/3/19/2241
About
On 9 January 2020, orphan designation EU/3/19/2241 was granted by the European Commission to ERA Consulting GmbH, Germany, for adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA (also known as ST-920) for the treatment of Fabry disease.
Key facts
Active substance |
adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA
|
Disease / condition |
Treatment of Fabry disease
|
Date of first decision |
09/01/2020
|
Outcome |
Positive
|
EU designation number |
EU/3/19/2241
|
Sponsor's contact details
ERA Consulting GmbH
Lange Strasse 70
29664 Walsrode
Germany
Tel. +49 5161 98900
E-mail: euagent@eraconsulting.com
Patients' organisations
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.