EU/3/19/2241

Table of contents

About

On 9 January 2020, orphan designation EU/3/19/2241 was granted by the European Commission to ERA Consulting GmbH, Germany, for adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA (also known as ST-920) for the treatment of Fabry disease.

Key facts

Active substance
adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA
Disease / condition
Treatment of Fabry disease
Date of first decision
09/01/2020
Outcome
Positive
EU designation number
EU/3/19/2241

Sponsor's contact details

ERA Consulting GmbH
Lange Strasse 70
29664 Walsrode
Germany
Tel. +49 5161 98900
E-mail: euagent@eraconsulting.com

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

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