On 9 January 2020, orphan designation EU/3/19/2241 was granted by the European Commission to ERA Consulting GmbH, Germany, for adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA (also known as ST-920) for the treatment of Fabry disease.
adeno-associated virus serotype 2/6 encoding human alpha-galactosidase A cDNA
|Disease / condition||
Treatment of Fabry disease
|Date of first decision||
|EU designation number||
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.