On 21 August 2020, orphan designation EU/3/20/2310 was granted by the European Commission to Institute for Ophthalmic Research, Germany, for adeno-associated virus serotype 2/8 vector containing the human PDE6A gene for the treatment of retinitis pigmentosa.
Adeno-associated virus serotype 2/8 vector containing the human PDE6A gene
|Disease / condition||
Treatment of retinitis pigmentosa
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.