EU/3/20/2310

About

On 21 August 2020, orphan designation EU/3/20/2310 was granted by the European Commission to Institute for Ophthalmic Research, Germany, for adeno-associated virus serotype 2/8 vector containing the human PDE6A gene for the treatment of retinitis pigmentosa.

Key facts

Active substance
Adeno-associated virus serotype 2/8 vector containing the human PDE6A gene
Disease / condition
Treatment of retinitis pigmentosa
Date of first decision
21/08/2020
Outcome
Positive
EU designation number
EU/3/20/2310

Review of designation

The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.

Sponsor's contact details

Institute For Ophthalmic Research
Elfriede-Aulhorn-Strasse 7
Nordstadt
72076 Tuebingen
Germany
Tel: + 4970712984920
E-mail: nadine.kahle@med.uni-tuebingen.de

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

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