EMEA-002122-PIP02-17

Key facts

Active substance
Adeno-associated viral vector serotype rh.10 carrying the humanNsulfoglucosamine Nsulfoglucosamine sulfohydrolase cDNA (LYS-SAF302)
Therapeutic area
Neurology
Decision number
P/0078/2018
PIP number
EMEA-002122-PIP02-17
Pharmaceutical form(s)
Solution for infusion
Condition(s) / indication(s)
Treatment of mucopolysaccharidosis type IIIA (Sanfilippo A syndrome)
Route(s) of administration
Intracerebral use
Contact for public enquiries
Lysogene
Tel. +1 6174448780
E-mail: sean.obryan@lysogene.com
Decision type
P: decision agreeing on a investigation plan, with or without partial waiver(s) and or deferral(s)

Decision

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