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529 results
Medicine type
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Human medicine European public assessment report (EPAR): Vyndaqel (updated)
tafamidis, Amyloidosis
Date of authorisation: 16/11/2011,
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, Revision: 14, Authorised, Last updated: 16/10/2019
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Human medicine European public assessment report (EPAR): Orphacol (updated)
cholic acid, Digestive System Diseases, Metabolism, Inborn Errors
Date of authorisation: 12/09/2013,
Date of refusal: 25/05/2012,, , , Revision: 7, Authorised, Last updated: 16/10/2019
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Human medicine European public assessment report (EPAR): Ofev (updated)
nintedanib, Idiopathic Pulmonary Fibrosis
Date of authorisation: 14/01/2015,
, , Revision: 11, Authorised, Last updated: 15/10/2019
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Human medicine European public assessment report (EPAR): Natpar (updated)
parathyroid hormone, Hypoparathyroidism
Date of authorisation: 24/04/2017,, , 
, Revision: 7, Authorised, Last updated: 14/10/2019
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Human medicine European public assessment report (EPAR): Symkevi (updated)
tezacaftor, ivacaftor, Cystic Fibrosis
Date of authorisation: 31/10/2018,, , Revision: 2, Authorised, Last updated: 14/10/2019
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Human medicine European public assessment report (EPAR): Kalydeco (updated)
ivacaftor, Cystic Fibrosis
Date of authorisation: 22/07/2012,, , Revision: 19, Authorised, Last updated: 14/10/2019
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Human medicine European public assessment report (EPAR): Xermelo (updated)
telotristat etiprate, Carcinoid Tumor, Neuroendocrine Tumors
Date of authorisation: 17/09/2017,, , Revision: 6, Authorised, Last updated: 11/10/2019
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Human medicine European public assessment report (EPAR): Ninlaro (updated)
ixazomib citrate, Multiple Myeloma
Date of authorisation: 21/11/2016,, , , Revision: 5, Authorised, Last updated: 10/10/2019
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Human medicine European public assessment report (EPAR): Ventavis (updated)
iloprost, Hypertension, Pulmonary
Date of authorisation: 15/09/2003,, Revision: 27, Authorised, Last updated: 10/10/2019
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Human medicine European public assessment report (EPAR): Tobi Podhaler (updated)
Tobramycin, Cystic Fibrosis, Respiratory Tract Infections
Date of authorisation: 20/07/2011,, Revision: 15, Authorised, Last updated: 09/10/2019
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Human medicine European public assessment report (EPAR): Besponsa (updated)
inotuzumab ozogamicin, Precursor Cell Lymphoblastic Leukemia-Lymphoma
Date of authorisation: 28/06/2017,, , Revision: 4, Authorised, Last updated: 09/10/2019
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Human medicine European public assessment report (EPAR): Procysbi (updated)
mercaptamine bitartrate, Cystinosis
Date of authorisation: 05/09/2013,, Revision: 12, Authorised, Last updated: 09/10/2019
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Human medicine European public assessment report (EPAR): Siklos (updated)
hydroxycarbamide, Anemia, Sickle Cell
Date of authorisation: 29/06/2007,, Revision: 17, Authorised, Last updated: 09/10/2019
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Human medicine European public assessment report (EPAR): Vyxeos (updated)
daunorubicin hydrochloride / cytarabine, Leukemia, Myeloid, Acute
Date of authorisation: 23/08/2018,, Revision: 1, Authorised, Last updated: 08/10/2019
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Human medicine European public assessment report (EPAR): Sylvant (updated)
siltuximab, EUSA Pharma (Netherlands) BV
Date of authorisation: 22/05/2014,, , , Revision: 10, Authorised, Last updated: 08/10/2019
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Human medicine European public assessment report (EPAR): Amglidia (updated)
glibenclamide, Diabetes Mellitus
Date of authorisation: 24/05/2018,, Revision: 3, Authorised, Last updated: 08/10/2019
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Human medicine European public assessment report (EPAR): Granupas (previously Para-aminosalicylic acid Lucane) (updated)
Para-aminosalicylic acid, Tuberculosis
Date of authorisation: 07/04/2014,, Revision: 7, Authorised, Last updated: 04/10/2019
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Human medicine European public assessment report (EPAR): Mepsevii (updated)
vestronidase alfa, Mucopolysaccharidosis VII
Date of authorisation: 23/08/2018,, , , Revision: 2, Authorised, Last updated: 03/10/2019
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Human medicine European public assessment report (EPAR): Ravicti (updated)
glycerol phenylbutyrate, Urea Cycle Disorders, Inborn
Date of authorisation: 26/11/2015,, , Revision: 11, Authorised, Last updated: 03/10/2019
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Human medicine European public assessment report (EPAR): Takhzyro (updated)
lanadelumab, Angioedemas, Hereditary
Date of authorisation: 22/11/2018,, , , Revision: 1, Authorised, Last updated: 01/10/2019
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Human medicine European public assessment report (EPAR): Tegsedi (updated)
inotersen sodium, Amyloidosis
Date of authorisation: 05/07/2018,, , , Revision: 3, Authorised, Last updated: 27/09/2019
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Human medicine European public assessment report (EPAR): Prevymis (updated)
Letermovir, Cytomegalovirus Infections
Date of authorisation: 08/01/2018,, , Revision: 5, Authorised, Last updated: 27/09/2019
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Human medicine European public assessment report (EPAR): Spinraza
nusinersen sodium, Muscular Atrophy, Spinal
Date of authorisation: 30/05/2017,, , , Revision: 8, Authorised, Last updated: 19/09/2019
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Human medicine European public assessment report (EPAR): Ketoconazole HRA
Ketoconazole, Cushing Syndrome
Date of authorisation: 18/11/2014,, , , Revision: 9, Authorised, Last updated: 18/09/2019
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Human medicine European public assessment report (EPAR): Firdapse (previously Zenas)
amifampridine, Lambert-Eaton Myasthenic Syndrome
Date of authorisation: 23/12/2009,, , , Revision: 17, Authorised, Last updated: 13/09/2019