89 results
Categories
Human Remove Human filter
-
List item
Orphan designation: stiripentol for: Treatment of severe myoclonic epilepsy in infancy
Date of first decision: 06/12/2001, Expired, Last updated: 08/02/2017 -
List item
Orphan designation: Iduronate-2-sulfatase for: Treatment of mucopolysaccharidosis type II (Hunter's syndrome)
Date of first decision: 11/12/2001, Expired, Last updated: 08/02/2017 -
List item
Orphan designation: dasatinib for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 23/12/2005, Expired, Last updated: 08/02/2017 -
List item
Orphan designation: dasatinib for: Treatment of chronic myeloid leukaemia
Date of first decision: 23/12/2005, Expired, Last updated: 08/02/2017 -
List item
Orphan designation: 3-(3-Methanesulfonyl-phenyl)-1-propyl-piperidine hydrochloride for: Treatment of narcolepsy
Date of first decision: 13/07/2016, Negative, Last updated: 09/01/2017 -
List item
Orphan designation: Naltrexone for: Treatment of fibromyalgia
Date of first decision: 06/10/2016, Negative, Last updated: 13/12/2016 -
List item
Orphan designation: 4-(3,5-Bis(hydroxy-phenyl)-1,2,4) triazol-1-yl) benzoic acid for: Treatment of chronic iron overload requiring chelation therapy
Date of first decision: 13/03/2002, Expired, Last updated: 30/09/2016 -
List item
Orphan designation: Dexrazoxane for: Treatment of anthracycline extravasations
Date of first decision: 19/09/2001, Expired, Last updated: 30/09/2016 -
List item
Orphan designation: 2-Chloro-9-[2-deoxy-2-fluoro-ß-D-arabinofuranosyl]adenine for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 05/02/2002, Expired, Last updated: 10/08/2016 -
List item
Orphan designation: Sorafenib tosilate for: Treatment of renal-cell carcinoma
Date of first decision: 29/07/2004, Expired, Last updated: 10/08/2016 -
List item
Orphan designation: Recombinant human acid alpha-glucosidase for: Treatment of glycogen storage disease type II (Pompe's disease)
Date of first decision: 15/02/2001, Expired, Last updated: 10/08/2016 -
List item
Orphan designation: N-acetylgalactosamine 4-sulfatase for: Treatment of mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)
Date of first decision: 15/02/2001, Expired, Last updated: 10/02/2016 -
List item
Orphan designation: sildenafil citrate for: Treatment of pulmonary arterial hypertension and chronic thromboembolic pulmonary hypertension
Date of first decision: 12/12/2003, Expired, Last updated: 19/01/2016 -
List item
Orphan designation: Nalbuphine hydrochloride for: Treatment of uraemic pruritus
Date of first decision: 27/02/2015, Negative, Last updated: 02/10/2015 -
List item
Orphan designation: nitisinone for: Treatment of tyrosinaemia type 1
Date of first decision: 30/12/2000, Expired, Last updated: 08/05/2015 -
List item
Orphan designation: ziconotide for: Treatment of chronic pain requiring intraspinal analgesia
Date of first decision: 09/07/2001, Expired, Last updated: 08/05/2015 -
List item
Orphan designation: 5-chloro-N2-[2-isopropoxy-5-methyl-4-(4-piperidinyl)phenyl]-N4-[2-(isopropylsulfonyl)phenyl]-2,4-pyrimidinediamine for: Treatment of non-small cell lung cancer (NSCLC) that is anaplastic lymphoma kinase (ALK)-positive
Date of first decision: 28/03/2014, Negative, Last updated: 10/03/2015 -
List item
Orphan designation: sodium ascorbate, menadione sodium bisulfite for: Treatment of autosomal dominant polycystic kidney disease
Date of first decision: 11/12/2014, Negative, Last updated: 10/03/2015 -
List item
Orphan designation: Zinc acetate dihydrate for: Treatment of Wilson's disease
Date of first decision: 31/07/2001, Expired, Last updated: 06/03/2015 -
List item
Orphan designation: Ibuprofen for: Treatment of patent ductus arteriosus
Date of first decision: 15/02/2001, Expired, Last updated: 06/03/2015 -
List item
Orphan designation: imatinib mesilate for: Treatment of chronic myeloid leukaemia
Date of first decision: 15/02/2001, Expired, Last updated: 10/02/2015 -
List item
Orphan designation: imatinib mesilate for: Treatment of acute lymphoblastic leukaemia
Date of first decision: 26/08/2005, Expired, Last updated: 10/02/2015 -
List item
Orphan designation: imatinib mesilate for: Treatment of malignant gastrointestinal stromal tumours
Date of first decision: 20/11/2001, Expired, Last updated: 09/02/2015 -
List item
Orphan designation: imatinib mesilate for: Treatment of myelodysplastic / myeloproliferative diseases
Date of first decision: 23/12/2005, Expired, Last updated: 09/02/2015 -
List item
Orphan designation: imatinib mesilate for: Treatment of dermatofibrosarcoma protuberans
Date of first decision: 26/08/2005, Expired, Last updated: 09/02/2015