94 results
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Orphan designation: Cysteamine hydrochloride for: Treatment of cystinosis
Date of designation: 07/11/2008, Positive, Last updated: 22/02/2017kezelése Italian Cisteamina cloridrato Trattamento della cistinosi … -
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Orphan designation: Enzastaurin hydrochloride for: Treatment of glioma
Date of designation: 23/12/2005, Positive, Last updated: 16/10/2020Leczenie glejaka Portuguese Cloridrato de enzastaurina Tratamento … -
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Orphan designation: 1-{3-[3-(4-Chlorophenyl)propoxy]propyl}piperidine, hydrochloride for: Treatment of narcolepsy
Date of designation: 10/07/2007, Positive, Last updated: 20/04/2016 -
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Orphan designation: 1-(4-(N-glycylamido)phenyl)-3-trifluoromethyl-5-(phenanthren-2-yl)-pyrazole-hydrochloride for: Treatment of tularaemia
Date of designation: 24/04/2015, Positive, Last updated: 21/05/2015 -
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Orphan designation: 1-(4-(N-glycylamido)phenyl)-3-trifluoromethyl-5-(phenanthren-2-yl)-pyrazole-hydrochloride for: Treatment of cryptococcosis
Date of designation: 24/04/2015, Positive, Last updated: 21/05/2015 -
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Orphan designation: Nilotinib hydrochloride monohydrate for: Treatment of gastrointestinal stromal tumours
Date of designation: 13/04/2007, Withdrawn, -
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Orphan designation: Glutathione-pegylated liposomal doxorubicin hydrochloride for: Treatment of glioma
Date of designation: 20/09/2010, Withdrawn, Last updated: 08/05/2015 -
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Orphan designation: Clonidine hydrochloride for: Prevention of oral mucositis in head and neck cancer patients undergoing radiation therapy
Date of designation: 27/10/2011, Positive, Last updated: 12/03/2015 -
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Orphan designation: Benserazide hydrochloride for: Treatment of beta thalassaemia intermedia and major
Date of designation: 16/12/2014, Positive, Last updated: 27/02/2015 -
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Orphan designation: Cysteamine hydrochloride for: Treatment of cystinosis
Date of designation: 15/10/2014, Positive, Last updated: 12/11/2014kezelése Italian Cisteamina cloridrato Trattamento della cistinosi … Leczenie cystynozy Portuguese Cloridrato de cisteamina Tratamento … -
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Orphan designation: Mexiletine hydrochloride for: Treatment of myotonic disorders
Date of designation: 07/10/2013, Positive, Last updated: 31/10/2013kezelése Italian Mexiletina cloridrato Trattamento dei disordini … -
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Orphan designation: Naloxone hydrochloride dihydrate for: Treatment of cutaneous T-cell lymphoma
Date of designation: 08/11/2012, Positive, Last updated: 13/12/2012 -
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Orphan designation: Xaliproden hydrochloride for: Treatment of amyotrophic lateral sclerosis
Date of designation: 17/01/2001, Withdrawn, Last updated: 06/05/2011σκλήρυνσης Italian Xaliproden cloridrato Trattamento della sclerosi … amiotrofica Portuguese Cloridrato de xaliprodeno Tratamento … -
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Orphan designation: apomorphine hydrochloride for: Treatment of moderate and severe traumatic brain injury
Date of designation: 13/05/2011, Positive, Last updated: 27/05/2011kezelése Italian Apomorfina cloridrato Trattamento delle lesioni … -
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Orphan designation: 17-(Allylamino)-17-demethoxygeldanamycin, hydroquinone hydrochloride for: Treatment of malignant gastrointestinal stromal tumours
Date of designation: 29/11/2007, Withdrawn, Last updated: 25/03/2011 -
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Orphan designation: Pazopanib hydrochloride for: Treatment of renal-cell carcinoma
Date of designation: 29/06/2006, Withdrawn, Last updated: 01/06/2011 -
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Orphan designation: raloxifene hydrochloride for: Treatment of hereditary haemorrhagic telangiectasia
Date of designation: 10/06/2010, Positive, Last updated: 24/06/2010 -
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Orphan designation: (S)-10-[(dimethylamino)methyl]-4-ethyl-9-hydroxy-4-O-[alpha-(2", 4", 5", 7"-tetranitro-9"-fluorenylideneaminooxy)propionyl]-1H-pyrano[3', 4', 6', 7']indolizino[1,2-beta]-quinoline-3, 14-(4H, 12H)-dione, hydrochloride for: Treatment of hepatocellular carcinoma
Date of designation: 01/10/2010, Positive, Last updated: 14/10/2010 -
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Orphan designation: Topotecan hydrochloride for: Treatment of glioma
Date of designation: 05/09/2008, Positive, Last updated: 24/04/2009 -
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Orphan designation: doxorubicin hydrochloride for: Treatment of soft tissue sarcoma
Date of designation: 27/10/2006, Positive, Last updated: 02/04/2009 -
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Orphan designation: Nemorubicin hydrochloride for: Treatment of hepatocellular carcinoma
Date of designation: 27/07/2005, Positive, Last updated: 27/10/2005kezelése Italian Nemorubicina cloridrato Trattamento del carcinoma … -
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Orphan designation: 1-Deoxygalactonojirimycin hydrochloride for: Treatment of Fabry disease
Date of designation: 22/05/2006, Positive, Last updated: 21/05/2019 -
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Orphan designation: Trans-N1-((1R,2S)-2-phenylcyclopropyl)cyclohexane-1,4-diamine bis-hydrochloride for: Treatment of acute myeloid leukaemia
Date of designation: 05/08/2013, Positive, Last updated: 05/02/2018 -
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Orphan designation: (-)-17(Cyclopropylmethyl)-1,14 beta-dihydroxy-4,5 alpha-epoxy-6beta-[N-methyl-trans-3-(3-furyl) acrylamido] morphinan hydrochloride (nalfurafine) for: Treatment of uraemic pruritus
Date of designation: 11/09/2002, Positive, Last updated: 14/02/2017 -
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Orphan designation: Sarizotan hydrochloride for: Treatment of Rett syndrome
Date of designation: 28/07/2015, Positive, Last updated: 18/08/2015zespołu Retta Portuguese Cloridrato de sarizotan Tratamento do …