European network of paediatric research-European Medicines Agency meeting on rare gastrointestinal and liver diseases
EventCorporateMedicines
Date
- Tuesday, 08 December 2015
Location
- European Medicines Agency, Amsterdam, the Netherlands
The European network of paediatric research (Enpr-EMA) is organising a one-day meeting. The morning session is dedicated to the Paediatric European Digestive Diseases Clinical Research Network (PEDDCReN) to present to industry representatives their planned initiative to prospectively identify the incidence and prevalence of rare and very rare diseases in the field of paediatric gastroenterology and hepatology by establishing a European registry for these rare diseases and to discuss with industry how best to use this to work for developing research in these unique groups of patients. The afternoon session is organised together with the European Cystic Fibrosis Society and will focus on gastrointestinal outcome measures for clinical trials with new medicines targeting the basic defect in cystic fibrosis, so-called CFTR modulators.