Spinal muscular atrophy workshop

Date: 11/11/2016
Location: European Medicines Agency, London

A one-day workshop on spinal muscular atrophy (SMA) co-organised by the European Medicines Agency, SMA Europe and TREAT NMD. The workshop brings together key stakeholders to discuss, help and advance the development of therapies for the treatment of SMA. Topics for discussion include an overview of the disease, the pharmacology of the molecules under investigation, natural history data, clinical outcome measures and biomarkers.



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