EU/3/20/2297: Orphan designation for the treatment of metachromatic leukodystrophy
Adeno-associated virus serotype HSC15 expressing human arylsulfatase A gene
Table of contents
Overview
On 26 June 2020, orphan designation EU/3/20/2297 was granted by the European Commission to YES Pharmaceutical Development Services GmbH, Germany, for adeno-associated virus serotype HSC15 expressing human arylsulfatase A gene (also known as HMI-202) for the treatment of metachromatic leukodystrophy.
Key facts
Active substance |
Adeno-associated virus serotype HSC15 expressing human arylsulfatase A gene
|
Intended use |
treatment of metachromatic leukodystrophy
|
Orphan designation status |
Withdrawn
|
EU designation number |
EU/3/20/2297
|
Date of designation |
26/06/2020
|
Sponsor |
Propharma Group The Netherlands B.V. |
Review of designation
The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.
Update history
Date | Update |
---|---|
July 2023 | Please note that this product was withdrawn from the Union Register of orphan medicinal products in July 2023 on request of the Sponsor. |
October 2022 | The sponsorship was transferred to Propharma Group The Netherlands B.V., Netherlands. |
June 2021 | The sponsorship was transferred to Diamond Pharma Services Ireland Limited, Ireland. |
Patients' organisations
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.
EU register of orphan medicines
The list of medicines that have received an orphan designation in the EU is available on the European Commission's website: