EU/3/01/018

Table of contents

About

Please note that this product was withdrawn from the Community Register of designated orphan medicinal products in March 2016 at the end of the period of market exclusivity.

On 14 February 2001, orphan designation (EU/3/01/018) was granted by the European Commission to Genzyme B.V., The Netherlands, for recombinant human acid α-glucosidase for the treatment of glycogen storage disease type II (Pompe's disease).

The sponsorship was transferred to Genzyme Europe BV, The Netherlands, in April 2002.

Update: recombinant human acid α-glucosidase has been authorised in the EU as Myozyme since 29 March 2006.

For a list of the administrative updates to this public summary of opinion please refer to the PDF document below.

Key facts

Active substance
Recombinant human acid alpha-glucosidase
Medicine name
Myozyme
Disease / condition
Treatment of glycogen storage disease type II (Pompe's disease)
Date of decision
15/02/2001
Outcome
Expired
Orphan decision number
EU/3/01/018

Sponsor's contact details

Genzyme Europe BV
Gooimeer 10
1411 DD Naarden
The Netherlands
Tel. +31 35 699 1200
Fax +31 35 694 3214
E-mail: eumedinfo@genzyme.com

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

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