On 17 December 2010, orphan designation (EU/3/10/818) was granted by the European Commission to Cytonet GmbH & Co. KG, Germany, for human heterologous liver cells (for infusion) for the treatment of citrullinaemia type 1.
The sponsorship was transferred to Promethera Biosciences, Belgium, in June 2016.
Human heterologous liver cells (for infusion)
|Disease / condition||
Treatment of citrullinaemia type 1
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
- Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
- European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.