On 9 February 2012, orphan designation (EU/3/12/954) was granted by the European Commission to University of Sheffield (SITraN), United Kingdom, for the treatment of amyotrophic lateral sclerosis.
The sponsorship was transferred to Granzer Regulatory Consulting & Services, Germany, in September 2019.
|Disease / condition||
Treatment of amyotrophic lateral sclerosis
|Date of first decision||
|EU designation number||
Review of designation
The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.