On 14 July 2016, orphan designation (EU/3/16/1706) was granted by the European Commission to Lucane Pharma SA, France, for sodium benzoate for the treatment of carbamoyl-phosphate synthase-1 deficiency.
|Disease / condition||
Treatment of carbamoyl-phosphate synthase-1 deficiency
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
- Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe;
- European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.