On 11 January 2019, orphan designation (EU/3/18/2125) was granted by the European Commission to Isabelle Ramirez, Germany, for benserazide hydrochloride for treatment of sickle cell disease.
The treatment of sickle cell disease
|Date of designation||
|Orphan designation status||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.