On 26 February 2019, orphan designation (EU/3/19/2136) was granted by the European Commission to Enzyvant Therapeutics Ireland Limited, Ireland, for allogeneic cultured postnatal thymus-derived tissue (also known as RVT-802) for the treatment of CHARGE syndrome.
Allogeneic cultured postnatal thymus-derived tissue
|Disease / condition||
Treatment of CHARGE syndrome
|Date of first decision||
|EU designation number||
Sponsor's contact details
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