On 1 April 2019, orphan designation (EU/3/19/2149) was granted by the European Commission to Brainvectis, France, for adeno-associated viral vector serotype rh10 containing the human cholesterol 24-hydroxylase gene for the treatment of Huntington's disease.
Adeno-associated viral vector serotype rh10 containing the human cholesterol 24-hydroxylase gene
|Disease / condition||
Treatment of Huntington’s disease
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.