On 24 April 2019, orphan designation (EU/3/19/2155) was granted by the European Commission to IQVIA RDS Ireland Limited, Ireland, for human culture expanded autologous mesenchymal stromal cells (also known as lenzumestrocel) for the treatment of amyotrophic lateral sclerosis.
Human culture expanded autologous mesenchymal stromal cells
|Disease / condition||
Treatment of amyotrophic lateral sclerosis
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.