On 25 July 2019, orphan designation EU/3/19/2187 was granted by the European Commission to Toleranzia AB, Sweden, for recombinant mutated extracellular domain of the human acetylcholine receptor subunit alpha1 for the treatment of myasthenia gravis.
Recombinant mutated extracellular domain of the human acetylcholine receptor subunit alpha1
|Disease / condition||
Treatment of myasthenia gravis
|Date of first decision||
|EU designation number||
Review of designation
Sponsor's contact details
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.