EMEA-001238-PIP03-21

Table of contents

Key facts

Active substance
Vatiquinone
Therapeutic area
Neurology
Decision number
P/0543/2021
PIP number
EMEA-001238-PIP03-21
Pharmaceutical form(s)
  • Oral solution
  • Capsule, hard
Condition(s) / indication(s)
Treatment of Friedreich's ataxia
Route(s) of administration
Oral use
Contact for public enquiries
PTC Therapeutics International Limited

Tel. +353 19068700
E-mail: medinfo@ptcbio.com

Decision type
P: decision agreeing on a investigation plan, with or without partial waiver(s) and or deferral(s)

Decision

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