EMEA-001244-PIP01-11-M02 - paediatric investigation plan
autologous haematopoietic stem cells transduced with lentiviral vector Lenti-D encoding the human ATP-binding cassette, sub-family D (ALD), member 1 (ABCD1) from cDNA
PIPHuman
Bluebird bio France
Tel. +1 41 415615437
E-mail: CDeCoster@bluebirdio.com