EMEA-001933-PIP01-16-M01
Key facts
| Active substance |
Autologous CD34+ cells transduced with lentiviral vector encoding the human beta-globin gene
|
| Therapeutic area |
Haematology-Hemostaseology
|
| Decision number |
P/0236/2020
|
| PIP number |
EMEA-001933-PIP01-16-M01
|
| Pharmaceutical form(s) |
Dispersion for injection
|
| Condition(s) / indication(s) |
Treatment of beta-thalassemia
|
| Route(s) of administration |
Intraosseous use
|
| Contact for public enquiries |
Fondazione Telethon ETS
E-mail: regulatory@telethon.it |
| Decision type |
P: decision agreeing on a investigation plan, with or without partial waiver(s) and or deferral(s)
|