EMEA-001933-PIP01-16-M01
Key facts
Active substance |
Autologous CD34+ cells transduced with lentiviral vector encoding the human beta-globin gene
|
Therapeutic area |
Haematology-Hemostaseology
|
Decision number |
P/0236/2020
|
PIP number |
EMEA-001933-PIP01-16-M01
|
Pharmaceutical form(s) |
Dispersion for injection
|
Condition(s) / indication(s) |
Treatment of beta-thalassemia
|
Route(s) of administration |
Intraosseous use
|
Contact for public enquiries |
Fondazione Telethon ETS
E-mail: regulatory@telethon.it |
Decision type |
P: decision agreeing on a investigation plan, with or without partial waiver(s) and or deferral(s)
|