On 26 October 2018, orphan designation (EU/3/18/2075) was granted by the European Commission to Consorcio Centro de Investigación Biomédica en Red, M.P., Spain, for gefinitib for the treatment of Fanconi anaemia.
The sponsor's name was updated in November 2022.
Treatment of Fanconi anaemia type A
|Orphan designation status||
|EU designation number||
|Date of designation||
Review of designation
|November 2022||The sponsor's name was updated.|
Documents related to this orphan designation evaluation
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.
EU register of orphan medicines
The list of medicines that have received an orphan designation in the EU is available on the European Commission's website: