EU/3/18/2075: Orphan designation for the treatment of Fanconi anaemia type A



On 26 October 2018, orphan designation (EU/3/18/2075) was granted by the European Commission to Consorcio Centro de Investigación Biomédica en Red, M.P., Spain, for gefinitib for the treatment of Fanconi anaemia.

The sponsor's name was updated in November 2022.

Key facts

Active substance
Intended use
Treatment of Fanconi anaemia type A
Orphan designation status
EU designation number
Date of designation

Consorcio Centro de Investigación Biomédica en Red
Instituto de Salud Carlos III
Pabellón 11, Planta 0
C/ Monforte de Lemos 3-5
28029 Madrid
Tel. +34 911 718 114

Review of designation

The Committee for Orphan Medicinal Products reviews the orphan designation of a product if it is approved for marketing authorisation.

Update history

Date Update
November 2022 The sponsor's name was updated.

Documents related to this orphan designation evaluation

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

EU register of orphan medicines

The list of medicines that have received an orphan designation in the EU is available on the European Commission's website:

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