EU/3/03/160 - orphan designation for treatment of retinopathy of prematurity

Antisense oligonucleotide (TATCCGGAGGGCTCGCCATGCTGCT)
OrphanHuman

Overview

Key facts

Active substance
Antisense oligonucleotide (TATCCGGAGGGCTCGCCATGCTGCT)
Intended use
Treatment of retinopathy of prematurity
Orphan designation status
Positive
EU designation number
EU/3/03/160
Date of designation
Sponsor

Gene Signal SAS
France

EMA list of opinions on orphan medicinal product designation

EMA publishes information on orphan medicinal product designation adopted by the Committee for Orphan Medicinal Products (COMP) on the IRIS online platform:

Patients' organisations

For contact details of patients’ organisations whose activities are targeted at rare diseases, see:

  • Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.

  • European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.

EU register of orphan medicines

The list of medicines that have received an orphan designation in the EU is available on the European Commission's website:

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