Overview
Key facts
- Active substance
- Antisense oligonucleotide (TATCCGGAGGGCTCGCCATGCTGCT)
- Intended use
- Treatment of retinopathy of prematurity
- Orphan designation status
- Positive
- EU designation number
- EU/3/03/160
- Date of designation
- Sponsor
Gene Signal SAS
France
EMA list of opinions on orphan medicinal product designation
EMA publishes information on orphan medicinal product designation adopted by the Committee for Orphan Medicinal Products (COMP) on the IRIS online platform:
Patients' organisations
For contact details of patients’ organisations whose activities are targeted at rare diseases, see:
Orphanet, a database containing information on rare diseases, which includes a directory of patients’ organisations registered in Europe.
European Organisation for Rare Diseases (EURORDIS), a non-governmental alliance of patient organisations and individuals active in the field of rare diseases.
EU register of orphan medicines
The list of medicines that have received an orphan designation in the EU is available on the European Commission's website: