Committee for Advanced Therapies (CAT) workshop on gene editing
Event
Human
Advanced therapies
- The original event time is:
- Tuesday, September 16, 2025 - 10:00 - 17:00 Amsterdam time (CEST)
Date
- , -
Location
- OnlineEuropean Medicines Agency, Amsterdam, the Netherlands
Event summary
This workshop, organised by CAT with the support of the Alliance for Regenerative Medicines (ARM), aims to identify current scientific and regulatory challenges of in vivo and in vitro gene editing (GE) medicines.
Input from the workshop assists the CAT in developing new guidance for these products.
During the morning session, academic experts provide general information on the different editors, the methods for off-target analysis, the state of clinical development and common challenges for clinical application of GE products. This is followed by a discussion session between CAT experts and GE developers.
In the afternoon, selected developers from industry and academia present to CAT their experience with GE medicinal product developments.
To safeguard the confidential information that is shared, some of the afternoon presentations are not open to the public. Only participants for Regulatory Authorities in EU are allowed to attend the closed sessions.